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Members of the ACT DMD Study Group Selected Research
Members of the ACT DMD Study Group Research Topics
Disease
1
Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker)
12/2021
Drug/Important Bio-Agent (IBA)
1
deflazacort
IBA
12/2021
1
ataluren
IBA
12/2021
1
Prednisolone (Predate)
FDA Link
Generic
12/2021
1
Prednisone (Sone)
FDA Link
Generic
12/2021
1
Nonsense Codon (Nonsense Mutation)
IBA
12/2021